Novel gene therapy platform speeds search for ways to cure blindness

A newly developed single-cell RNA sequencing technique enables researchers to quickly identify an optimal vector for delivering therapeutic genetic material to treat vision disorders, and perhaps other genetic conditions.

A collaboration among scientists from the University of Pennsylvania, University of Pittsburgh School of Medicine, University of California, Berkeley, and Carnegie Mellon University has developed a platform to identify top-performing viral vectors that could deliver gene therapies to the retina with maximum efficiency and precision.

Read more in Penn Today

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